Therapeutic Exon Skipping Through a CRISPR-Guided Cytidine Deaminase Rescues Dystrophic Cardiomyopathy in Vivo | |
论文作者 | Li, J; Wang, KY; Zhang, YC; Qi, T; Yuan, JJ; Zhang, L; Qiu, H; Wang, JX; Yang, HT; Dai, Y; Song, Y; Chang, X |
期刊/会议名称 | CIRCULATION |
论文年度 | 2021 |
论文类别 | Article |
期 | 22 |
卷 | 144 |
影响因子 | 29.69 |