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Therapeutic Exon Skipping Through a CRISPR-Guided Cytidine Deaminase Rescues Dystrophic Cardiomyopathy in Vivo
论文作者 Li, J; Wang, KY; Zhang, YC; Qi, T; Yuan, JJ; Zhang, L; Qiu, H; Wang, JX; Yang, HT; Dai, Y; Song, Y; Chang, X
期刊/会议名称 CIRCULATION
论文年度 2021
论文类别 Article
22
144
影响因子 29.69